Approval of two gene therapies - USA
December 18 , 2023
343 days
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- The U.S. FDA has approved two gene therapies - Casgevy and Lyfgenia - to treat sickle cell disease in patients over 12.
- Its decision on approving Casgevy gene therapy for treating beta thalassemia is expected by March 2024.
- These decisions mark the beginning of gene therapy using the CRISPR-Cas9 tool to treat diseases.
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